Sarepta Therapeutics demanded a prominent patient advocacy organization censor a video that contained pointed criticism of the company’s recently approved gene therapy for Duchenne muscular dystrophy, ...

Duchenne muscular dystrophy (DMD) is a genetic disease in which muscle cells fail to produce a protein called dystrophin. Unlike some other forms of muscular dystrophy, in Duchenne there is a complete ...

Werner is CEO of Alltrna and CEO-partner at Flagship Pioneering. Duchenne muscular dystrophy has seen more progress in the past 15 months (give or take) than in the last couple of decades combined. In ...

Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed down) disorder. The condition is linked ...

More than 30 rare muscular dystrophy types cause progressive muscle weakness from inherited gene mutations. Combined, they affect about 1 in 5,000 to 8,000 people. Common subtypes vary by age of onset ...

A new treatment platform developed by researchers at the University of Texas MD Anderson Cancer Center was able to deliver ...

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine Today, the world stands at a crossroads in genetic medicine ...

Dear Mayo Clinic: What is Duchenne muscular dystrophy, and what causes it? Is treatment available? Can Duchenne muscular dystrophy be cured? Muscular dystrophy is an umbrella term applied to a group ...

Today’s hottest genome-engineering method, CRISPR-Cas9, has recently been used to treat mouse models of the most common form of muscular dystrophy, Duchenne’s muscular dystrophy (DMD). Three groups of ...

Duchenne muscular dystrophy (DMD) is an X-linked recessive disorder affecting 1 in every 5000 live male births caused by mutations in the DMD gene [1]. Muscle degeneration is apparent as early as 2–5 ...

This quick alphabetical guide will help you feel more confident when talking about muscular dystrophy with your doctor and loved ones. Muscular dystrophy is the name for a group of genetic diseases ...